Notice of Special Interest (NOSI): Pre-Clinical Research on Gene Therapies for Rare Genetic Neurodevelopmental Disorders
Department of Health and Human Services ▸ National Institutes of Health ▸
Description
The NIMH is supporting research to develop and test technologies and methods for creating gene therapies aimed at treating rare neurodevelopmental disorders. This involves different gene therapy approaches like replacing, adding, editing, or silencing genes. The goal is to gather preclinical data using cell or animal experiments to evaluate the safety and effectiveness of these potential treatments.
The NIMH is encouraging research to establish, optimize, and evaluate technologies and assays needed for the clinical development of somatic cell gene therapies to treat rare neurodevelopmental disorders. This includes gene replacement, addition, editing, and silencing. The focus is on obtaining…
Source
Grant ID
NOT-MH-23-236
Funding Source
Department of Health and Human Services ▸ National Institutes of Health ▸
Key Dates
Opportunity Released
April 28, 2023
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